Resources for Your Practice
Support tools to help you navigate treatment decisions and patient care with confidence
For You and Your Team
Start your eligible patients on SEPHIENCE
Download and complete the Prescription Start Form, then fax it to PTC Cares™ to begin the process.
Dosing and Administration Guide
Step-by-step instructions, key considerations, and best practices to help ensure proper dosing and patient adherence.
PTC Cares: Together, We’ve Got This
Helping patients with PKU access treatment
PTC Cares is a personalized support program committed to helping members of the rare disease community. We’re here to help make the process of getting treatment easier on your patients.
PTC Cares will work to remove financial obstacles so your patients can access the PKU therapies you prescribe. We offer dedicated support programs to assist eligible families with treatment costs.
The Copay Assistance Program*†
The Bridge Program*
Patient Assistance Program (PAP)
PKU Quick Start Program
For more information, please reach out to your PTC Therapeutics Account Manager.
*Low to no out-of-pocket costs for most patients who qualify.
†Not valid for prescriptions eligible to be reimbursed, in whole or in part, by Medicaid or Medicare (including Medicare Part D), or where prohibited by law.
Not actual patients.
Advocacy Groups
Here are some organizations and resources that could help your patients on their journey. Remind your PKU patients and caregivers: support is out there—resources, communities, and local groups are a great place to start.
National PKU Alliance
National PKU Alliance (NPKUA) is the only national organization dedicated solely to supporting individuals and families affected by PKU. NPKUA provides trusted, up-to-date information on treatment and research, while building connection through community calls, peer mentoring, and life-stage support kits. They also advance progress in PKU research through a PKU patient registry and direct investment in scientific innovation.
flok
flok supports those living with PKU and their caregivers by providing an app for daily PKU management, annual family camps, educational resources, and the opportunity to drive research through daily care. Care and Research, Together. That’s flok.
National Organization for Rare Disorders (NORD)
NORD offers the latest information about PKU research and care, as well as financial assistance for patients and resources to connect with the rare disease community.
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PKU: Phenylketonuria.